Title of article
The Pathway from Gene Therapy to Genome Editing: A Nightmare or Dream
Author/Authors
Hasanzad, Mandana Medical Genomics Research Center - Tehran Medical Sciences - Islamic Azad University, Tehran , Larijani, Bagher Personalized Medicine Research Center - Endocrinology and Metabolism Clinical Sciences Institute - Tehran University of Medical Sciences, Tehran
Pages
2
From page
69
To page
70
Abstract
The gene therapy approach has largely been improved by the development of new methods in gene transfer and genome editing. The use of CART cells was first approved in 2018 by FDA for ex vivo treatment of B cell acute lymphoblastic leukemia and in vivo treatment of retinal dystrophy. This revolutionary trend is expected to continue as the clinical vision develops and the technical capacity improves.
Keywords
Gene Therapy , Genome Editing
Journal title
Astroparticle Physics
Serial Year
2019
Record number
2485169
Link To Document